FDA Approves First Drug To Treat Alexander Disease After 30 Years of Research
Ionis began the human trial in the summer of 2021, evaluating the treatment’s efficacy and safety in 54 patients at 13 sites ...
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Alexander disease: FDA approves first drug that can target the root cause of the rare neurological disease
The US Food and Drug Administration (FDA) recently approved the first drug for Alexander disease, a rare and progressive neurological disorder. Alexander disease is marked by symptoms like seizures, ...
MedCity News
FDA Approves Ionis Pharma Drug, the First for Ultra-Rare Alexander Disease
The neurological deterioration and progressive muscle weakness caused by Alexander disease now have their first FDA-approved therapy, a genetic medicine that Ionis Pharmaceuticals designed to address ...