That’s a longstanding issue with rare-disease drug candidates, given the inherently small patient base available for trials. McCarthy said the panel’s input would be helpful as the FDA ...

The UK's regulator has granted early access to Alnylam's ultra-rare disease drug lumasiran, allowing patients with primary hyperoxaluria type 1 to gain access ahead of a regulatory decision ...

A talented LEGO fan with an affection for Pokemon builds an impressively detailed custom model of the legendary Pokemon Ho-Oh. LEGO Pokemon ... appears to be a super rare Xbox 360 console variant ...

Lugia, Ho-Oh, and Suicune get a cute makeover with baby forms designed by a skilled Pokemon fan artist. The baby versions of ...

Opinions expressed by Forbes Contributors are their own. I'm a New Yorker who grew up next to a garage, and became obsessed. Barry Skolnick’s The Ikonick Collection is one of the most renowned ...

A woman born with an ultra rare condition that causes grapefruit-sized tumors has revealed her latest health fears after having multiple surgeries. Leanna Scaglione, 32, first discovered she had ...

However, Tennessee’s Victor Sharrah sees monsters everywhere due to an ultra-rare condition called “demon face” syndrome that causes everyone to look like they have an evil smile ...

Prequalify now It only takes a couple minutes and won't affect your credit. Used This is my third GX. I love everything about this car. It drives wonderfully and I love all the extra features it has.

A rare 1982 911 Turbo Slantnose is currently up ... but customization divisions are nothing new. Porsche’s ultra-exclusive Sonderwunsch special requests program has been catering to the marque ...

Even though the Bottomless Trap Hole allows you to counter a special summon above 1500 ATK, when Premature Burial is used you cannot counter it. Jaden Yuki's favorite card is glitched in the game ...

Prequalify now It only takes a couple minutes and won't affect your credit. Used This is my 4th Lexus 460 GX. It seems smaller and there no point using the 3rd row no leg room. What I don't like ...