pharmaphorum1y
ultra-rare diseases
The UK's regulator has granted early access to Alnylam's ultra-rare disease drug lumasiran, allowing patients with primary hyperoxaluria type 1 to gain access ahead of a regulatory decision ...
Politico15d
An opening for an ultra-rare disease drug
That’s a longstanding issue with rare-disease drug candidates, given the inherently small patient base available for trials. McCarthy said the panel’s input would be helpful as the FDA ...
Daily Mail3d
Woman, 32, born with ultra rare condition that sees her grow lumps as big as GRAPEFRUITS reveals her latest health fears after multiple surgeries
A woman born with an ultra rare condition that causes grapefruit-sized tumors has revealed her latest health fears after having multiple surgeries. Leanna Scaglione, 32, first discovered she had ...
Daily Mail26d
Incredible moment ultra-rare Livingstone's fruit bat gives birth upside down is caught on camera for first time ever in British zoo
Watch the incredible moment an ultra-rare fruit bat is filmed giving birth upside down at a British zoo for the first time ever. The critically endangered Livingstone's fruit bat, Selene ...
Hosted on MSN1mon
81-year-old who carried rare ‘stone baby’ inside her for over 50 years dies after surgery to remove it
A n 81-year-old pensioner named Daniela Almeida Vera passed away in Brazil after undergoing surgery to remove an ultra-rare “stone baby,” which she had been carrying inside her for ...
New York Post1mon
This is what it’s like to have scary ‘demon face’ syndrome, a rare condition that makes everyone look Satanic
However, Tennessee’s Victor Sharrah sees monsters everywhere due to an ultra-rare condition called “demon face” syndrome that causes everyone to look like they have an evil smile ...
Yahoo24d
This Ultra-Rare Porsche 911 Was the First of Its Kind in the U.S. and Now It’s up for Grabs
A rare 1982 911 Turbo Slantnose is currently up ... but customization divisions are nothing new. Porsche’s ultra-exclusive Sonderwunsch special requests program has been catering to the marque ...
Forbes6mon
Ultra-Rare 2014 McLaren P1 Goes To Auction Today At Sotheby’s Motorsport
Opinions expressed by Forbes Contributors are their own. I'm a New Yorker who grew up next to a garage, and became obsessed. Barry Skolnick’s The Ikonick Collection is one of the most renowned ...
Forbes1mon
February 29 Has Been A Rare Yet Interesting Date In Baseball Finance
So it is “rare ... 29, 2016, in Cleveland where ownership opened the purse strings for a different $4 million payout. It all went to 37-year-old infielder Juan Uribe. He hit .206 in 73 ...
The Citizen1mon
February 29 is Rare Disease Day
Rare Disease Day, observed globally on the last day of February each year, serves as an essential platform for uniting patients, their families, caregivers, medical professionals, researchers ...
The Washington Post8d
Ericsson: Q1 Earnings Snapshot
STOCKHOLM — STOCKHOLM — Ericsson (ERIC) on Tuesday reported first-quarter net income of $246.2 million. The Stockholm-based company said it had net income of 7 cents per share. The results ...