Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Recent research takes aim at the a variant in gene SCN1B, which causes a severe form of developmental epileptic encephalopathy.
Researchers developed a new gene-editing strategy that dramatically boosts the effectiveness of gene therapies in the liver, a breakthrough that could lead to new treatments for about 700 genetic ...
Congestive heart failure (CHF) and heart failure are the same thing. Both terms describe the inability of the heart to pump enough blood to service the body's needs. The term "congestive" simply ...
Heart disease is more common in people over 65, but treatments are better than ever. That can complicate decision-making for ...
Researchers from Heidelberg University, Heidelberg University Hospital (UKHD) and Heidelberg Institute for Theoretical ...
Researchers developed an epigenetic editing approach to silence the PCSK9 gene, achieving long-term cholesterol reduction ...
Tech entrepreneur Bryan Johnson has made headlines for his ambitious anti-ageing experiments. In a recent appearance on Realign podcast, he claimed that one can successfully reverse the biological age ...
PDE2 (phosphodiesterase 2) is upregulated in human heart failure. Cardiac PDE2‐transgenic mice are ... function and its putative beneficial effects in HF, we performed gene therapy with ...
This FDA-approved therapy is based ... a virus engineered not to cause disease but rather to deliver a gene capable of producing the missing TNAP enzyme and reversing the malformation of bones ...
The trial linked the use of the cell therapy to a slowdown in ALS disease progression over the first three months. However, the pace of deterioration returned to its pretreatment rate at the 6 ...
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